ATXN7

ataxin 7

Summary

The autosomal dominant cerebellar ataxias (ADCA) are a heterogeneous group of neurodegenerative disorders characterized by progressive degeneration of the cerebellum, brain stem and spinal cord. Clinically, ADCA has been divided into three groups: ADCA types I-III. ADCAI is genetically heterogeneous, with five genetic loci, designated spinocerebellar ataxia (SCA) 1, 2, 3, 4 and 6, being assigned to five different chromosomes. ADCAII, which always presents with retinal degeneration (SCA7), and ADCAIII often referred to as the 'pure' cerebellar syndrome (SCA5), are most likely homogeneous disorders. Several SCA genes have been cloned and shown to contain CAG repeats in their coding regions. ADCA is caused by the expansion of the CAG repeats, producing an elongated polyglutamine tract in the corresponding protein. The expanded repeats are variable in size and unstable, usually increasing in size when transmitted to successive generations. This locus has been mapped to chromosome 3, and it has been determined that the diseased allele associated with spinocerebellar ataxia-7 contains 37-306 CAG repeats (near the N-terminus), compared to 4-35 in the normal allele. The encoded protein is a component of the SPT3/TAF9/GCN5 acetyltransferase (STAGA) and TBP-free TAF-containing (TFTC) chromatin remodeling complexes, and it thus plays a role in transcriptional regulation. Alternative splicing results in multiple transcript variants. [provided by RefSeq, Jul 2016]

Known Variants107 total

rsidPosition (GRCh37)AllelesClassClinVar
rs67793723:63,850,298T/A
rs8321923:63,853,423T/A
rs731170423:63,896,543T/Cintron variant
rs5574456103:63,898,311C/Tuncertain significance
rs14788913783:63,898,328G/Clikely benign
rs21072960863:63,898,330C/Auncertain significance
rs21072961993:63,898,353G/Auncertain significance
rs7670668613:63,898,375A/Cuncertain significance
rs7729182443:63,898,378A/Clikely benign
rs9290409133:63,898,385G/Cuncertain significance
rs7608874743:63,898,398C/Tuncertain significance
rs17040936843:63,898,401C/Guncertain significance
rs15758834233:63,898,417A/Guncertain significance
rs7555081213:63,898,453C/Guncertain significance
rs15758835273:63,898,455G/Cuncertain significance
rs7472710543:63,898,465G/Cuncertain significance
rs2015612863:63,898,485T/Glikely benign
rs13706623953:63,898,491G/Auncertain significance
rs1996639153:63,898,497A/Tuncertain significance
rs11712616053:63,898,504C/Guncertain significance
rs14188425093:63,898,522C/Tuncertain significance
rs2013346183:63,898,547G/Cbenign
rs3755860943:63,938,063A/Guncertain significance
rs3699993323:63,938,097A/Guncertain significance
rs24713849403:63,938,148A/Cuncertain significance
rs560158753:63,965,583A/Glikely benign
rs3761660983:63,965,629G/Aconflicting classifications of pathogenicity
rs24714547793:63,965,655C/Guncertain significance
rs2018552363:63,965,675G/Auncertain significance
rs14154887433:63,965,723T/Cuncertain significance
rs7509565453:63,965,725C/Guncertain significance
rs7552348903:63,965,730C/Guncertain significance
rs24714549763:63,965,738C/Tuncertain significance
rs3686476433:63,965,781G/Cuncertain significance
rs1999136433:63,965,786G/Alikely benign
rs2005642243:63,965,830C/Tuncertain significance
rs24714605363:63,967,872T/Guncertain significance
rs9579044763:63,967,881G/Auncertain significance
rs10533383:63,967,900A/Gbenign
rs20755013233:63,967,950A/Cuncertain significance
rs8632233933:63,967,953G/Abenign
rs20755018963:63,967,982C/Guncertain significance
rs24714610033:63,967,984G/Auncertain significance
rs1402707873:63,968,025A/Tconflicting classifications of pathogenicity
rs3721711563:63,968,032A/Cuncertain significance
rs9484163753:63,968,052C/Tuncertain significance
rs1473684003:63,968,089A/Guncertain significance
rs1834964773:63,968,134T/Alikely benign
rs13661239763:63,973,801G/Auncertain significance
rs21067802053:63,973,859C/Guncertain significance
rs3752593173:63,973,861C/Tuncertain significance
rs617365703:63,973,888G/Alikely benign
rs7729955403:63,973,927C/Tuncertain significance
rs3776626893:63,973,987C/Tuncertain significance
rs11872432013:63,975,860G/Auncertain significance
rs3764551623:63,975,907G/Cuncertain significance
rs7739380643:63,975,919C/Tuncertain significance
rs20756489333:63,975,973G/Auncertain significance
rs9858718083:63,975,974G/Auncertain significance
rs7798604023:63,975,976G/Auncertain significance
rs3683446243:63,976,030C/Tuncertain significance
rs9916575343:63,976,447G/Auncertain significance
rs2013787073:63,976,466C/Guncertain significance
rs3701895753:63,976,478G/Auncertain significance
rs7806037643:63,976,483C/Tuncertain significance
rs15759979963:63,976,491C/Auncertain significance
rs1807049423:63,976,512G/Abenign
rs1832310743:63,981,237G/Auncertain significance
rs3677729983:63,981,248G/Auncertain significance
rs1995143763:63,981,335C/Guncertain significance
rs7816273283:63,981,338A/Guncertain significance
rs20757465443:63,981,383C/Tuncertain significance
rs1386401613:63,981,399C/Tuncertain significance
rs5298116753:63,981,473C/Tuncertain significance
rs11814703933:63,981,489C/Tuncertain significance
rs8659554323:63,981,582C/Tuncertain significance
rs13377581543:63,981,617C/Alikely pathogenic
rs3689177113:63,981,618G/Auncertain significance
rs7488477773:63,981,633C/Tuncertain significance
rs37331253:63,981,635T/Cbenign
rs11780092313:63,981,651C/Guncertain significance
rs7708771703:63,981,657C/Guncertain significance
rs21068048003:63,981,668T/Alikely benign
rs617365673:63,981,676C/Tlikely benign
rs7485086443:63,981,728C/Tuncertain significance
rs7782325883:63,981,737C/Guncertain significance
rs3760738823:63,981,744C/Tuncertain significance
rs24715004283:63,981,753C/Guncertain significance
rs12847359103:63,981,764A/Guncertain significance
rs1996761653:63,981,799G/Alikely benign
rs7575698133:63,981,806G/Cuncertain significance
rs7662128153:63,981,836C/Tuncertain significance
rs7576919323:63,981,864A/Guncertain significance
rs617365683:63,981,902C/Guncertain significance
rs1454562633:63,981,933A/Cuncertain significance
rs7500139283:63,981,941C/Tuncertain significance
rs1870430983:63,981,949C/Alikely benign
rs7810680163:63,981,957G/Aconflicting classifications of pathogenicity
rs1472595093:63,981,977A/Glikely benign
rs9419768433:63,981,995A/Guncertain significance

Showing 100 of 107 variants. Use the SNP search for the full list.

Gene information from NCBI Gene. Variant classifications from ClinVar.