GFRA1

GDNF family receptor alpha 1

Summary

This gene encodes a member of the glial cell line-derived neurotrophic factor receptor (GDNFR) family of proteins. The encoded preproprotein is proteolytically processed to generate the mature receptor. Glial cell line-derived neurotrophic factor (GDNF) and neurturin (NTN) are two structurally related, potent neurotrophic factors that play key roles in the control of neuron survival and differentiation. This receptor is a glycosylphosphatidylinositol (GPI)-linked cell surface receptor for both GDNF and NTN, and mediates activation of the RET tyrosine kinase receptor. This gene is a candidate gene for Hirschsprung disease. Alternative splicing results in multiple transcript variants, at least one of which encodes a preproprotein that is proteolytically processed. [provided by RefSeq, Jan 2016]

Known Variants54 total

rsidPosition (GRCh37)AllelesClassClinVar
rs37402027910:117,823,915T/Clikely benign
rs7584123810:117,823,963C/Glikely benign
rs230210510:117,824,888C/A
rs37105278310:117,825,076A/Clikely benign
rs7625344810:117,825,106T/Clikely benign
rs76903400010:117,825,118T/Guncertain significance
rs14328580510:117,849,279A/Tuncertain significance
rs18858981110:117,849,304C/Guncertain significance
rs207227610:117,849,353T/Cbenign
rs249541261910:117,849,412C/Tuncertain significance
rs19993982610:117,853,226G/Abenign
rs37202819910:117,856,157G/Alikely benign
rs14731161210:117,856,185G/Alikely benign
rs77924982510:117,856,198G/Tuncertain significance
rs77256967410:117,856,199C/Tuncertain significance
rs36936129710:117,856,215A/Glikely benign
rs13888695610:117,856,242C/Auncertain significance
rs75456246210:117,856,264G/Auncertain significance
rs86322333210:117,856,267A/Guncertain significance
rs118481424810:117,856,270C/Tuncertain significance
rs37623932710:117,884,727C/Alikely benign
rs13863313410:117,884,747G/Alikely benign
rs14842129910:117,884,748T/Cuncertain significance
rs7624833810:117,884,755G/Alikely benign
rs133354366310:117,884,777T/Cuncertain significance
rs19181408610:117,884,826G/Alikely pathogenic
rs100553715410:117,884,831C/Tuncertain significance
rs20033458710:117,884,852C/Tlikely benign
rs249575894610:117,884,869C/Tuncertain significance
rs74613842810:117,884,874C/Apathogenic
rs92703429410:117,884,892G/Auncertain significance
rs76155476910:117,884,934G/Auncertain significance
rs224502010:117,884,950G/Abenign
rs13998497410:117,884,951T/Cuncertain significance
rs76426168610:117,885,052T/Clikely benign
rs1119757110:117,942,634A/Gintron variant
rs14620774510:117,955,500G/Aintron variant
rs1088587710:117,966,090C/A
rs269476510:117,967,763T/Cintron variant
rs36953436310:117,971,143C/Guncertain significance
rs1241335510:117,973,597A/Gintron variant
rs107926110:117,986,910G/Aintron variant
rs426984710:117,991,102A/Gintron variant
rs15074146710:118,007,752G/Aintron variant
rs7550376610:118,023,295G/Aintron variant
rs249386160210:118,029,071T/Cuncertain significance
rs249387573110:118,030,343T/Cuncertain significance
rs3437126210:118,030,386C/Tbenign
rs119722526010:118,030,411T/Cuncertain significance
rs819266210:118,030,415A/Tbenign
rs131834760710:118,030,468T/Cuncertain significance
rs7653114510:118,030,627T/Gbenign
rs37215649110:118,030,633G/Tlikely benign
rs158993058110:118,031,541T/Auncertain significance

Gene information from NCBI Gene. Variant classifications from ClinVar.